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Rett Syndrome Genetic Medicines Summit 2023

We are at a pivotal moment in drug development where the first genetic medicines have entered the clinic and the possibility of achieving cures for Rett is tangible.

In mid September 2023 the Rett Syndrome Research Trust hosted a pioneering meeting, the Rett Syndrome Genetic Medicines Summit. The first meeting of its kind to be organized with biopharmaceutical companies front and center, the Summit gathered basic science, pre-clinical, clinical, and regulatory experts to foster discussion, refine expectations, and identify best practices to expedite genetic medicine development. Our expectations are that the information shared at the meeting and beyond will be a rising tide that lifts all boats and will move us closer to a future without Rett.

Read Summit Press Release.

Rett Syndrome Genetic Medicines Summit 2023

Summit Program Book

RSRT invited 130 scientists and clinicians from 20 academic institutions, 43 biopharmaceutical companies, NIH and FDA to participate at the Summit via presentations, panel discussions and poster session.

Featured Speakers

Adrian Bird, PhD
Adrian Bird, PhD
Buchanan Chair of Genetics, University of Edinburgh
Stuart Cobb, PhD
Stuart Cobb, PhD
University of Edinburgh, Chief Scientific Officer, Neurogene
David R. Liu, PhD
David R. Liu, PhD
Richard Merkin Professor, Broad Institute of MIT and Harvard, HHMI
Peter Marks, MD, PhD
Peter Marks, MD, PhD
Director, Center for Biologics Evaluation and Research, FDA
Sukumar Nagendran, MD
Sukumar Nagendran, MD
President and Head of R&D, Taysha Gene Therapies
Huda Zoghbi, MD
Huda Zoghbi, MD
Baylor College of Medicine, HHMI, The Jan and Dan Duncan Neurological Research Institute

Sponsors